About Remix Therapeutics
Remix Therapeutics focuses on creating treatments for rare and difficult diseases, particularly targeting rare cancers and genetic disorders. Their main product, REM 422, is an oral small molecule that works by degrading messenger RNA (mRNA), which can stop the production of harmful proteins linked to these diseases. Currently, REM 422 is undergoing Phase 1 clinical trials for Adenoid Cystic Carcinoma and Acute Myeloid Leukemia, and it has received Orphan Drug Designation from the FDA, which offers benefits for drugs treating rare conditions. Unlike many competitors, Remix Therapeutics emphasizes a strong research and development approach, funding their work through grants and partnerships, with the goal of bringing new medicines to patients inspired by personal experiences with serious illnesses.